P104: BASE EDITING REPAIRS THE HBE MUTATION RESTORING THE PRODUCTION OF NORMAL GLOBIN CHAINS IN SEVERE HBE/β‐THALASSEMIA PATIENT HEMATOPOIETIC STEM AND ERYTHROID CELLS
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Published in: | HemaSphere 2022-01, Vol.6 (Suppl), p.19-20 |
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Main Authors: | , , , , , , , , |
Format: | Article |
Language: | eng |
Subjects: | |
Online Access: | Get full text |
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Summary: | |
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ISSN: | 2572-9241 2572-9241 |