Recombination-activating gene 1 ( Rag1 )–deficient mice with severe combined immunodeficiency treated with lentiviral gene therapy demonstrate autoimmune Omenn-like syndrome by van Til, Niek P., PhD, Sarwari, Roya, MSc, Visser, Trudi P., BSc, Hauer, Julia, MD, Lagresle-Peyrou, Chantal, PhD, van der Velden, Guus, BSc, Malshetty, Vidyasagar, PhD, Cortes, Patricia, PhD, Jollet, Arnaud, PhD, Danos, Olivier, PhD, Cassani, Barbara, PhD, Zhang, Fang, PhD, Thrasher, Adrian J., MD, PhD, Fontana, Elena, PhD, Poliani, Pietro L., MD, PhD, Cavazzana, Marina, MD, PhD, Verstegen, Monique M.A., PhD, Villa, Anna, MD, PhD, Wagemaker, Gerard, PhD

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Reply by van Til, Niek P., PhD, Cortes, Patricia, PhD, Danos, Olivier, PhD, Cassani, Barbara, PhD, Poliani, Pietro L., MD, PhD, Villa, Anna, MD, PhD, Wagemaker, Gerard, PhD

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