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Search Results - Zaccariotto, Eva
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A novel brain-penetrant oral UGT8 inhibitor decreases in vivo galactosphingolipid biosynthesis in murine Krabbe disease
by
Zaccariotto, Eva
,
Cachón-González, María Begoña
,
Wang, Bing
,
Lim, Sungtaek
,
Hirth, Bradford
,
Park, Hyejung
,
Fezoui, Malika
,
Sardi, S.Pablo
,
Mason, Paul
,
Barker, Robert H.
,
Cox, Timothy M.
Published in
Biomedicine & pharmacotherapy
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76. In situ brain perfusion in a mouse model of Sanfilippo syndrome
by
Pontikis, Charles
,
Zaccariotto, Eva
Published in
Molecular genetics and metabolism
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Gene therapy approaches for lysosomal storage disorders, a good model for the treatment of mendelian diseases
by
Tomanin, Rosella
,
Zanetti, Alessandra
,
Zaccariotto, Eva
,
D'Avanzo, Francesca
,
Bellettato, Cinzia M
,
Scarpa, Maurizio
Published in
Acta Paediatrica
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First evidence of efficacy in brain following intravenous injections of Brain-Targeted Liposome-Enzyme in the MPS II mouse model
by
Scarpa, Maurizio
,
Zaccariotto, Eva
,
D'Avanzo, Francesca
,
van Weperen, Willem
,
Rip, Jaap
,
Gaillard, Pieter
,
Tomanin, Rosella
Published in
Molecular genetics and metabolism
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In vivo delivery of naked antisense oligos in aged mdx mice: Analysis of dystrophin restoration in skeletal and cardiac muscle
by
Vitiello, Libero
,
Bassi, Nicola
,
Campagnolo, Paola
,
Zaccariotto, Eva
,
Occhi, Gianluca
,
Malerba, Alberto
,
Pigozzo, Sarah
,
Reggiani, Carlo
,
Ausoni, Simonetta
,
Zaglia, Tania
,
Gamba, Piergiorgio
,
Baroni, Maurizio D
,
Ditadi, Andrea P
Published in
Neuromuscular disorders : NMD
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Rapid diagnostic of multidrug-resistant sepsis pathogens directly from blood culture bottles using MALDI-TOF and the EUCAST RAST
by
Pariona, Jesus G.M.
,
Oliveira, Flavio A.
,
Scoton, Patrícia Helena
,
Barrón-Pastor, Heli J.
,
Pariona, Eva M.M.
,
Zaccariotto, Tania R.
,
Lincopan, Nilton
,
Levy, Carlos E.
Published in
Diagnostic microbiology and infectious disease
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Molecular Genetics And Metabolism
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Acta Paediatrica
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