Twice‐weekly glucocorticosteroids in infants and young boys with Duchenne muscular dystrophy by Connolly, Anne M., Zaidman, Craig M., Golumbek, Paul T., Cradock, Mary M., Flanigan, Kevin M., Kuntz, Nancy L., Finkel, Richard S., McDonald, Craig M., Iannaccone, Susan T., Anand, Pallavi, Siener, Catherine A., Florence, Julaine M., Lowes, Linda P., Alfano, Lindsay N., Johnson, Linda B., Nicorici, Alina, Nelson, Leslie L., Mendell, Jerry R.

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Outcome reliability in non-Ambulatory Boys/Men with duchenne muscular dystrophy by Connolly, Anne M., Malkus, Elizabeth C., Mendell, Jerry R., Flanigan, Kevin M., Miller, J. Philip, Schierbecker, Jeanine R., Siener, Catherine A., Golumbek, Paul T., Zaidman, Craig M., Mcdonald, Craig M., Johnson, Linda, Nicorici, Alina, Karachunski, Peter I., Day, John W., Kelecic, Jason M., Lowes, Linda P., Alfano, Lindsay N., Darras, Basil T., Kang, Peter B., Quigley, Janet, Pasternak, Amy E., Florence, Julaine M.

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Motor and cognitive assessment of infants and young boys with Duchenne Muscular Dystrophy: results from the Muscular Dystrophy Association DMD Clinical Research Network by Connolly, Anne M, Florence, Julaine M, Cradock, Mary M, Malkus, Elizabeth C, Schierbecker, Jeanine R, Siener, Catherine A, Wulf, Charlie O, Anand, Pallavi, Golumbek, Paul T, Zaidman, Craig M, Philip Miller, J, Lowes, Linda P, Alfano, Lindsay N, Viollet-Callendret, Laurence, Flanigan, Kevin M, Mendell, Jerry R, McDonald, Craig M, Goude, Erica, Johnson, Linda, Nicorici, Alina, Karachunski, Peter I, Day, John W, Dalton, Joline C, Farber, Janey M, Buser, Karen K, Darras, Basil T, Kang, Peter B, Riley, Susan O, Shriber, Elizabeth, Parad, Rebecca, Bushby, Kate, Eagle, Michelle

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Clinical trial readiness in non-ambulatory boys and men with duchenne muscular dystrophy: MDA-DMD network follow-up by Connolly, Anne M., Florence, Julaine M., Zaidman, Craig M., Golumbek, Paul T., Mendell, Jerry R., Flanigan, Kevin M., Karachunski, Peter I., Day, John W., McDonald, Craig M., Darras, Basil T., Kang, Peter B., Siener, Catherine A., Gadeken, Rebecca K., Anand, Pallavi, Schierbecker, Jeanine R., Malkus, Elizabeth C., Lowes, Linda P., Alfano, Lindsay N., Johnson, Linda, Nicorici, Alina, Kelecic, Jason M., Quigley, Janet, Pasternak, Amy E., Miller, J. Philip

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Electrical impedance myography in duchenne muscular dystrophy and healthy controls: A multicenter study of reliability and validity by Zaidman, Craig M., Wang, Lucy L., Connolly, Anne M., Florence, Julaine, Wong, Brenda L., Parsons, Julie A., Apkon, Susan, Goyal, Namita, Williams, Eugene, Escolar, Diana, Rutkove, Seward B., Bohorquez, Jose L.

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LTBP4 genotype predicts age of ambulatory loss in duchenne muscular dystrophy by Flanigan, Kevin M., Ceco, Ermelinda, Lamar, Kay-Marie, Kaminoh, Yuuki, Dunn, Diane M., Mendell, Jerry R., King, Wendy M., Pestronk, Alan, Florence, Julaine M., Mathews, Katherine D., Finkel, Richard S., Swoboda, Kathryn J., Gappmaier, Eduard, Howard, Michael T., Day, John W., McDonald, Craig, McNally, Elizabeth M., Weiss, Robert B.

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Mutational spectrum of DMD mutations in dystrophinopathy patients: application of modern diagnostic techniques to a large cohort by Flanigan, Kevin M, Dunn, Diane M, von Niederhausern, Andrew, Soltanzadeh, Payam, Gappmaier, Eduard, Howard, Michael T, Sampson, Jacinda B, Mendell, Jerry R, Wall, Cheryl, King, Wendy M, Pestronk, Alan, Florence, Julaine M, Connolly, Anne M, Mathews, Katherine D, Stephan, Carrie M, Laubenthal, Karla S, Wong, Brenda L, Morehart, Paula J, Meyer, Amy, Finkel, Richard S, Bonnemann, Carsten G, Medne, Livija, Day, John W, Dalton, Joline C, Margolis, Marcia K, Hinton, Veronica J, Weiss, Robert B

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Association Study of Exon Variants in the NF-κB and TGFβ Pathways Identifies CD40 as a Modifier of Duchenne Muscular Dystrophy by Bello, Luca, Flanigan, Kevin M., Weiss, Robert B., Dunn, Diane M., Swoboda, Kathryn J., Gappmaier, Eduard, Howard, Michael T., Sampson, Jacinda B., Bromberg, Mark B., Butterfield, Russell, Kerr, Lynne, Pestronk, Alan, Florence, Julaine M., Connolly, Anne, Lopate, Glenn, Golumbek, Paul, Schierbecker, Jeanine, Malkus, Betsy, Renna, Renee, Siener, Catherine, Finkel, Richard S., Bonnemann, Carsten G., Medne, Livija, Glanzman, Allan M., Flickinger, Jean, Mendell, Jerry R., King, Wendy M., Lowes, Linda, Alfano, Lindsay, Mathews, Katherine D., Stephan, Carrie, Laubenthal, Karla, Baldwin, Kris, Wong, Brenda, Morehart, Paula, Meyer, Amy, Day, John W., Naughton, Cameron E., Margolis, Marcia, Spitali, Pietro, Aartsma-Rus, Annemieke, Muntoni, Francesco, Zaharieva, Irina, Ferlini, Alessandra, Mercuri, Eugenio, Tuffery-Giraud, Sylvie, Claustres, Mireille, Straub, Volker, Lochmüller, Hanns, Barp, Andrea, Vianello, Sara, Pegoraro, Elena, Punetha, Jaya, Gordish-Dressman, Heather, Giri, Mamta, McDonald, Craig M., Hoffman, Eric P., Cnaan, Avital, Abresch, Richard T., Henricson, Erik K., Morgenroth, Lauren P., Duong, Tina, Chidambaranathan, V. Viswanathan, Biggar, W. Douglas, McAdam, Laura C., Mah, Jean, Tulinius, Mar, Leshner, Robert, Rocha, Carolina Tesi, Thangarajh, Mathula, Kornberg, Andrew, Ryan, Monique, Nevo, Yoram, Dubrovsky, Alberto, Clemens, Paula R., Abdel-Hamid, Hoda, Connolly, Anne M., Teasley, Jean, Bertorini, Tulio E., North, Kathryn, Webster, Richard, Kolski, Hanna, Kuntz, Nancy, Driscoll, Sherilyn, Carlo, Jose, Gorni, Ksenija, Lotze, Timothy, Karachunski, Peter, Bodensteiner, John B.

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Nonsense mutation-associated Becker muscular dystrophy: interplay between exon definition and splicing regulatory elements within the DMD gene by Flanigan, Kevin M, Dunn, Diane M, von Niederhausern, Andrew, Soltanzadeh, Payam, Howard, Michael T, Sampson, Jacinda B, Swoboda, Kathryn J, Bromberg, Mark B, Mendell, Jerry R, Taylor, Laura E, Anderson, Christine B, Pestronk, Alan, Florence, Julaine M, Connolly, Anne M, Mathews, Katherine D, Wong, Brenda, Finkel, Richard S, Bonnemann, Carsten G, Day, John W, McDonald, Craig, Weiss, Robert B

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One Year Outcome of Boys With Duchenne Muscular Dystrophy Using the Bayley-III Scales of Infant and Toddler Development by Connolly, Anne M., MD, Florence, Julaine M., PT, DPT, Cradock, Mary M., PHD, Eagle, Michelle, PhD, MSc, MCSP, Flanigan, Kevin M., MD, McDonald, Craig M., MD, Karachunski, Peter I., MD, Darras, Basil T., MD, Bushby, Kate, MD, Malkus, Elizabeth C., PT, MHS, Golumbek, Paul T., MD, PhD, Zaidman, Craig M., MD, Miller, J. Philip, PhD, Mendell, Jerry R., MD

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Clinical trial readiness in non-ambulatory boys and men with duchenne muscular dystrophy: MDA-DMD network follow-up: Twelve and 24-Month Outcomes in DMD by Connolly, Anne M., Florence, Julaine M., Zaidman, Craig M., Golumbek, Paul T., Mendell, Jerry R., Flanigan, Kevin M., Karachunski, Peter I., Day, John W., McDonald, Craig M., Darras, Basil T., Kang, Peter B., Siener, Catherine A., Gadeken, Rebecca K., Anand, Pallavi, Schierbecker, Jeanine R., Malkus, Elizabeth C., Lowes, Linda P., Alfano, Lindsay N., Johnson, Linda, Nicorici, Alina, Kelecic, Jason M., Quigley, Janet, Pasternak, Amy E., Miller, J. Philip

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Physical frailty and body composition in obese elderly men and women by Villareal, D.T, Banks, M, Siener, C, Sinacore, D.R, Klein, S

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Optimizing hand-function patient outcome measures for inclusion body myositis by Lin, Ava Yun, Siener, Catherine Sly, Faino, Anna V., Seiffert, Michelle, Weihl, Conrad C, Wang, Leo H.

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Assessing the Relationship of Patient Reported Outcome Measures With Functional Status in Dysferlinopathy: A Rasch Analysis Approach by Mayhew, Anna G, James, Meredith K, Moore, Ursula, Sutherland, Helen, Jacobs, Marni, Feng, Jia, Lowes, Linda Pax, Alfano, Lindsay N, Muni Lofra, Robert, Rufibach, Laura E, Rose, Kristy, Duong, Tina, Bello, Luca, Pedrosa-Hernández, Irene, Holsten, Scott, Sakamoto, Chikako, Canal, Aurélie, Sánchez-Aguilera Práxedes, Nieves, Thiele, Simone, Siener, Catherine, Vandevelde, Bruno, DeWolf, Brittney, Maron, Elke, Gordish-Dressman, Heather, Hilsden, Heather, Guglieri, Michela, Hogrel, Jean-Yves, Blamire, Andrew M, Carlier, Pierre G, Spuler, Simone, Day, John W, Jones, Kristi J, Bharucha-Goebel, Diana X, Salort-Campana, Emmanuelle, Pestronk, Alan, Walter, Maggie C, Paradas, Carmen, Stojkovic, Tanya, Mori-Yoshimura, Madoka, Bravver, Elena, Díaz-Manera, Jordi, Pegoraro, Elena, Mendell, Jerry R, Straub, Volker

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Performance of upper limb entry item to predict forced vital capacity in dysferlin-deficient limb girdle muscular dystrophy by Borland, Holly, Moore, Ursula, Dressman, Heather Gordish, Human, Anri, Mayhew, Anna G., Hilsden, Heather, Rufibach, Laura E., Duong, Tina, Maron, Elke, DeWolf, Brittney, Rose, Kristy, Siener, Catherine, Thiele, Simone, Práxedes, Nieves Sanchez-Aguilera, Canal, Aurélie, Holsten, Scott, Sakamoto, Chikako, Pedrosa-Hernández, Irene, Bello, Luca, Alfano, Lindsay N, Lowes, Linda Pax, James, Meredith K., Straub, Volker

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Assessing Dysferlinopathy Patients Over Three Years With a New Motor Scale by Jacobs, Marni B., James, Meredoith K., Lowes, Linda P., Alfano, Lindsay N., Eagle, Michelle, Muni Lofra, Robert, Moore, Ursula, Feng, Jia, Rufibach, Laura E., Rose, Kristy, Duong, Tina, Bello, Luca, Pedrosa‐Hernández, Irene, Holsten, Scott, Sakamoto, Chikako, Canal, Aurélie, Sanchez‐Aguilera Práxedes, Nieves, Thiele, Simone, Siener, Catherine, Vandevelde, Bruno, DeWolf, Brittney, Maron, Elke, Guglieri, Michela, Hogrel, Jean‐Yves, Blamire, Andrew M., Carlier, Pierre G., Spuler, Simone, Day, John W., Jones, Kristi J., Bharucha‐Goebel, Diana X., Salort‐Campana, Emmanuelle, Pestronk, Alan, Walter, Maggie C., Paradas, Carmen, Stojkovic, Tanya, Mori‐Yoshimura, Madoka, Bravver, Elena, Díaz‐Manera, Jordi, Pegoraro, Elena, Mendell, Jerry R., Mayhew, Anna G., Straub, Volker

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Fixed dynamometry is more sensitive than vital capacity or ALS rating scale by Andres, Patricia L., Allred, Margaret (Peggy), Stephens, Helen E., Proffitt Bunnell, Mary, Siener, Catherine, Macklin, Eric A., Haines, Travis, English, Robert A., Fetterman, Katherine A., Kasarskis, Edward J., Florence, Julaine, Simmons, Zachary, Cudkowicz, Merit E.

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Qualitative and quantitative skeletal muscle ultrasound in late-onset acid maltase deficiency by Zaidman, Craig M., Malkus, Elizabeth C., Siener, Catherine, Florence, Julaine, Pestronk, Alan, Al-Lozi, Muhammad

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Developing normalized strength scores for neuromuscular research by Andres, Patricia L., English, Robert, Mendoza, Michelle, Florence, Julaine, Malkus, Elizabeth, Schierbecker, Jeanine, Siener, Catherine, Malspeis, Susan, Schoenfeld, David A., Munsat, Theodore L., Cudkowicz, Merit E.

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