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A protein domain-oriented approach to expand the opportunities of therapeutic exon skipping for USH2A-associated retinitis pigmentosa
by
Schellens, Renske T.W.
,
Broekman, Sanne
,
Peters, Theo
,
Graave, Pam
,
Malinar, Lucija
,
Venselaar, Hanka
,
Kremer, Hannie
,
De Vrieze, Erik
,
Van Wijk, Erwin
Published in
Molecular therapy. Nucleic acids
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Molecular Therapy. Nucleic Acids
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Antisense Oligonucleotides
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Crispr-Cas9
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Dual Exon Skipping
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Life Sciences & Biomedicine
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Medicine, Research & Experimental
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Mt: Oligonucleotides: Therapies And Applications
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Original
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Photoreceptors
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Research & Experimental Medicine
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Retinitis Pigmentosa
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Science & Technology
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Ush2A
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Zebrafish
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