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Search Results - Northcutt, Valerie J.
Search Results - Northcutt, Valerie J.
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Phase 2a study of ataluren-mediated dystrophin production in patients with nonsense mutation Duchenne muscular dystrophy
by
Finkel, Richard S
,
Flanigan, Kevin M
,
Wong, Brenda
,
Bönnemann, Carsten
,
Sampson, Jacinda
,
Sweeney, H Lee
,
Reha, Allen
,
Northcutt, Valerie J
,
Elfring, Gary
,
Barth, Jay
,
Peltz, Stuart W
Published in
PloS one
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Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations: a prospective phase II trial
by
Kerem, Eitan, Dr
,
Hirawat, Samit, MD
,
Armoni, Shoshana, BSN
,
Yaakov, Yasmin, MSc
,
Shoseyov, David, MD
,
Cohen, Michael, MD
,
Nissim-Rafinia, Malka, PhD
,
Blau, Hannah, MD
,
Rivlin, Joseph, MD
,
Aviram, Micha, MD
,
Elfring, Gary L, MS
,
Northcutt, Valerie J, MS
,
Miller, Langdon L, MD
,
Kerem, Batsheva, PhD
,
Wilschanski, Michael, MBBS
Published in
The Lancet (British edition)
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Safety, Tolerability, and Pharmacokinetics of PTC124, a Nonaminoglycoside Nonsense Mutation Suppressor, Following Single- and Multiple-Dose Administration to Healthy Male and Femal...
by
Hirawat, Samit
,
Welch, Ellen M.
,
Elfring, Gary L.
,
Northcutt, Valerie J.
,
Paushkin, Sergey
,
Hwang, Seongwoo
,
Leonard, Eileen M.
,
Almstead, Neil G.
,
Ju, William
,
Peltz, Stuart W.
,
Miller, Langdon L.
Published in
Journal of clinical pharmacology
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PTC124 targets genetic disorders caused by nonsense mutations
by
Chen, Guangming
,
Jacobson, Allan
,
Spatrick, Phyllis
,
Peltz, Stuart W
,
Conn, M. Morgan
,
Friesen, Westley J
,
Almstead, Neil G
,
Hedrick, Jean
,
Campbell, Jeffrey A
,
Mollin, Anna
,
Kawana, Masataka
,
Wilde, Richard G
,
Yeh, Shirley
,
Sweeney, H. Lee
,
Trotta, Christopher R
,
Khan, Atiyya
,
Welch, Ellen M
,
Barton, Elisabeth R
,
Hirawat, Samit
,
Turpoff, Anthony A
,
Weetall, Marla
,
Ren, Hongyu
,
Risher, Nicole
,
Tomizawa, Yuki
,
Northcutt, Valerie J
,
Miller, Langdon L
,
He, Feng
,
Jones, Stephen
,
Colacino, Joseph M
,
Feng, Huisheng
,
Branstrom, Arthur A
,
Corson, Donald
,
Zhuo, Jin
,
Ju, William D
,
Patel, Meenal
,
Moon, Young-Choon
,
Hwang, Seongwoo
,
Paushkin, Sergey
,
Babiak, John
,
Trifillis, Panayiota
,
Karp, Gary
,
Takasugi, James
Published in
Nature
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Phase 2a Study of Ataluren-Mediated Dystrophin Production in Patients with Nonsense Mutation Duchenne Muscular Dystrophy: e81302
by
Finkel, Richard S
,
Flanigan, Kevin M
,
Wong, Brenda
,
Bonnemann, Carsten
,
Sampson, Jacinda
,
Sweeney, H Lee
,
Reha, Allen
,
Northcutt, Valerie J
,
Elfring, Gary
,
Barth, Jay
Published in
PloS one
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Effectiveness of PTC124 treatment of cystic fibrosis caused by nonsense mutations : a prospective phase II trial. Commentary
by
HYDE, Stephen C
,
GILL, Deborah R
,
RIVLIN, Joseph
,
AVIRAM, Micha
,
ELFRING, Gary L
,
NORTHCUTT, Valerie J
,
MILLER, Langdon L
,
KEREM, Batsheva
,
WILSCHANSKI, Michael
,
KEREM, Eitan
,
HIRAWAT, Samit
,
ARMONI, Shoshana
,
YAAKOV, Yasmin
,
SHOSEYOV, David
,
COHEN, Michael
,
NISSIM-RAFINIA, Malka
,
BLAU, Hannah
Published in
The Lancet (British edition)
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