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Search Results - Modrzejewska, Sandra
Search Results - Modrzejewska, Sandra
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Safety and efficacy of once-daily risdiplam in type 2 and non-ambulant type 3 spinal muscular atrophy (SUNFISH part 2): a phase 3, double-blind, randomised, placebo-controlled tria...
by
Nascimento, Andres
,
Vuillerot, Carole
,
Boespflug-Tanguy, Odile
,
Kirschner, Janbernd
,
Kostera-Pruszczyk, Anna
,
Kletzl, Heidemarie
,
Day, John W
,
Volpe, Joseph J.
,
Posner, John
,
Daron, Aurore
,
Delbeke, Patricia
,
Wittevrongel, Sylvia
,
De Vos, Elke
,
De Waele, Liesbeth
,
Prufer de Queiroz Campos Araujo, Alexandra
,
Haefeli, Lorena
,
Chiu, Angela
,
Oskoui, Maryam
,
Toffoli, Daniela
,
Turgeon Desilets, Sarah
,
Wang, Yi
,
Shen, Li
,
Li, Hui
,
Sang, Tian
,
Barisic, Nina
,
Galiot Delic, Martina
,
Ivkic, Petra Kristina
,
Kern, Ivana
,
Momtchilova, Marta Milkova
,
Milascevic, Darko
,
Aubertin, Guillaume
,
Coopman, Stephanie
,
Debruyne, Philippe
,
Derlyn, Gilles
,
Danjoux, Loïc
,
Deladrière, Élodie
,
Germa, Virginie
,
Billaud, Fanny
,
Le Goff, Lucie
,
Letellier, Guy
,
De-Montferrand, Camille
,
Le-Goff, Laure
,
Fontaine, Stephanie
,
Kirschner, Janbernd
,
Lagréze, Wolf
,
Bertini, Enrico
,
D'Amico, Adele
,
Carlesi, Adelina
,
Zuffi, Ambra
,
Comi, Giacomo Pietro
,
Daniele, Velardo
,
Minorini, Valeria
,
Fassini, Federica
,
Foa, Michaela
,
Parente, Valeria
,
Masson, Riccardo
,
Tremolada, Gemma
,
Amorelli, Giulia Maria
,
Orazi, Lorenzo
,
Coratti, Giorgia
,
Morishita, Yuko
,
Goto, Miwako
,
Tsutsui, Saki
,
Takatsuji, Yuta
,
Komaki, Hirofumi
,
Omori, Miina
,
Nagura, Hiroe
,
Usui, Manami
,
Fudeyasu, Kenishi
,
Hirata, Kazuhiko
,
Michiue, Kana
,
Fujitani, Junko
,
Seki, Maiko
,
Fukuyama, Koji
,
Shibata, Minoru
,
Kobayashi, Kyoko
,
Nakamura, Yukie
,
Sikorski, Adam
,
Koberda, Mateusz
,
Stodolska-Koberda, Urszula
,
Waskowska, Agnieszka
,
Kolendo, Jagoda
,
Steinborn, Barbara
,
Klimas, Monika
,
Stopa, Marcin
,
Gajewska, Ewa
,
Leppenen, Natalya
,
Brankovic, Vesna
,
Djokic, Olivera
,
Planas Pascual, Bernat
,
Salinas, Marta Peña
,
Padros, Nuria
,
Oncel, Ibrahim
,
Eroglu Ertugru, Nesibe
,
Kadayifçilar, Sibel
,
Karaduman, Aynur Ayse
,
Chiriboga, Claudia
,
Marquet, Anne
,
Muelhardt, Nicoletta
,
Trundell, Dylan
Published in
Lancet neurology
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Sitting in patients with spinal muscular atrophy type 1 treated with nusinersen
by
Aragon‐Gawinska, Karolina
,
Daron, Aurore
,
Ulinici, Ana
,
Vanden Brande, Laura
,
Seferian, Andreea
,
Gidaro, Teresa
,
Scoto, Mariacristina
,
Deconinck, Nicolas
,
Servais, Laurent
,
Benezit, Audrey
,
Mathieu, Marie‐Laure
,
Cances, Claude
,
Durigneux, Julien
,
Ropars, Juliette
,
Chouchane, Mondher
,
Forey, Peggy
,
Lazaro, Leila
,
Hughes, Imelda
,
Illingworth, Marjorie
,
Marini‐Bettolo, Chiara
,
Cuppen, Inge
,
Modrzejewska, Sandra
,
Balintova, Zdenka
,
Haberlova, Jana
,
Drimtzia, Kate
,
Blaschek, Astrid
,
Ambegankoar, Gautam
,
Annoussamy, Melanie
Published in
Developmental medicine and child neurology
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Safety and efficacy of risdiplam in patients with type 1 spinal muscular atrophy (FIREFISH part 2): secondary analyses from an open-label trial
by
Masson, Riccardo
,
Mazurkiewicz-Bełdzińska, Maria
,
Xiong, Hui
,
Bruno, Claudio
,
Day, John W
,
Deconinck, Nicolas
,
Klein, Andrea
,
Mercuri, Eugenio
,
Wang, Yi
,
Dodman, Angela
,
Gaki, Eleni
,
Posner, John
,
Kellner, Ulrich
,
Quinlivan, Rosaline
,
Khwaja, Omar
,
Scalco, Renata S
,
Seabrook, Timothy
,
Koch, Armin
,
Balikova, Irina
,
Tahon, Valentine
,
De Vos, Elke
,
de Holanda Mendonça, Rodrigo
,
Machado, Cleide
,
Polido, Graziela
,
Hu, Chaoping
,
Qian, Chen
,
Li, Hui
,
Zhou, Shuizhen
,
Zhou, Zhenxuan
,
Wei, Cuijie
,
Dong, Hui
,
Wen, Jing
,
Qin, Lun
,
Celovec, Ivan
,
Galiot Delic, Martina
,
Ivkic, Petra Kristina
,
Vukojevic, Nenad
,
Kern, Ivana
,
Boespflug-Tanguy, Odile
,
De Lucia, Silvana
,
Barreau, Emmanuel
,
Mnafek, Nabila
,
Peche, Helene
,
Pagliano, Emanuela
,
Bianchi Marzoli, Stefania
,
Santarsiero, Diletta
,
Tremolada, Gemma
,
Vigano, Marta
,
Dosi, Claudia
,
Zanin, Riccardo
,
Schembri, Veronica
,
Brolatti, Noemi
,
Rao, Giuseppe
,
Tassara, Elisa
,
Sposetti, Lorenza
,
Govoni, Alessandra
,
Osnaghi, Silvia Gabriella
,
Minorini, Valeria
,
Abbati, Francesca
,
Fassini, Federica
,
Foa, Michaela
,
Lopopolo, Amalia
,
Pane, Marika
,
Palermo, Concetta
,
Barresi, Costanza
,
Orazi, Lorenzo
,
Laura, Antonaci
,
De Sanctis, Roberto
,
Berti, Beatrice
,
Kimura, Naoki
,
Shimomura, Hideki
,
Lee, Tomoko
,
Morimatsu, Takanobu
,
Waskowska, Agnieszka
,
Kolendo, Jagoda
,
Sobierajska-Rek, Agnieszka
,
Modrzejewska, Sandra
,
Lemska, Anna
,
Melnik, Evgenia
,
Leppenen, Natalya
,
Papina, Yulia
,
Shidlovsckaia, Olga
,
Enzmann, Cornelia
,
Wondrusch Haschke, Christine
,
Topaloglu, Haluk
,
Oncel, Ibrahim
,
Ertugrul, Nesibe Eroglu
,
Konuskan, Bahadir
,
Alemdaroglu, Ipek
,
Sari, Seher
,
Karaduman, Aynur Ayse
,
Graham, Robert J
,
Ghosh, Partha
,
Levine, Alexis
,
Engelbrekt, Amanda
,
Ambrosio, Lucia
,
Baglieri, Anna Maria
,
Maczek, Elizabeth
,
Duong, Tina
,
Young, Sally
Published in
Lancet neurology
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Peri-ictal headaches in the paediatric population – prospective study
by
Zawadzka, Marta
,
Pilarska, Ewa
,
Konieczna, Seweryna
,
Szmuda, Marta
,
Matheisel, Agnieszka
,
Lemska, Anna
,
Modrzejewska, Sandra
,
Mazurkiewicz-Bełdzińska, Maria
Published in
Cephalalgia
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The signifficance of focal EEG abnormalities in typical absence seizures – Long term observations
by
Mazurkiewicz-Bełdzińska, Maria
,
Szmuda, Marta
,
Zawadzka, Marta
,
Pawłowicz, Małgorzata
,
Matheisel, Agnieszka
,
Modrzejewska, Sandra
Published in
European journal of paediatric neurology
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