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Search Results - Mendizabal, Macarena Rodriguez
Search Results - Mendizabal, Macarena Rodriguez
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European Medicines Agency review of ataluren for the treatment of ambulant patients aged 5 years and older with Duchenne muscular dystrophy resulting from a nonsense mutation in th...
by
Haas, Manuel
,
Vlcek, Viktor
,
Balabanov, Pavel
,
Salmonson, Tomas
,
Bakchine, Serge
,
Markey, Greg
,
Weise, Martina
,
Schlosser-Weber, Gabriele
,
Brohmann, Henning
,
Yerro, Concepcion Prieto
,
Mendizabal, Macarena Rodriguez
,
Stoyanova-Beninska, Violeta
,
Hillege, Hans L
Published in
Neuromuscular disorders : NMD
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Neuromuscular Disorders : Nmd
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116978-02-0
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775304-57-9
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775304-59-1
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Adolescent
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Adult
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Ataluren
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Child
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Child, Preschool
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Clinical Neurology
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Clinical Trials, Phase Ii As Topic
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Codon, Nonsense
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Drug Approval
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Duchenne Muscular Dystrophy
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Dystrophin
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Dystrophin - Genetics
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Dystrophin Gene
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Humans
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Life Sciences & Biomedicine
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Male
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Muscular Dystrophy, Duchenne - Drug Therapy
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