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Search Results - McDougald, Devin S
Search Results - McDougald, Devin S
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AAV2.7m8 is a powerful viral vector for inner ear gene therapy
by
Isgrig, Kevin
,
McDougald, Devin S
,
Zhu, Jianliang
,
Wang, Hong Jun
,
Bennett, Jean
,
Chien, Wade W
Published in
Nature communications
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SIRT1 and NRF2 Gene Transfer Mediate Distinct Neuroprotective Effects Upon Retinal Ganglion Cell Survival and Function in Experimental Optic Neuritis
by
McDougald, Devin S
,
Dine, Kimberly E
,
Zezulin, Alexandra U
,
Bennett, Jean
,
Shindler, Kenneth S
Published in
Investigative ophthalmology & visual science
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Cochlear gene transfer mediated by adeno-associated virus: Comparison of two surgical approaches
by
Chien, Wade W.
,
McDougald, Devin S.
,
Roy, Soumen
,
Fitzgerald, Tracy S.
,
Cunningham, Lisa L.
Published in
The Laryngoscope
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Selective Upregulation of SIRT1 Expression in Retinal Ganglion Cells by AAV-Mediated Gene Delivery Increases Neuronal Cell Survival and Alleviates Axon Demyelination Associated wit...
by
Ross, Ahmara G
,
Chaqour, Brahim
,
McDougald, Devin S
,
Dine, Kimberly E
,
Duong, Thu T
,
Shindler, Ryan E
,
Yue, Jipeng
,
Liu, Tehui
,
Shindler, Kenneth S
Published in
Biomolecules (Basel, Switzerland)
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Spliceosome-Mediated Pre-mRNA trans-Splicing Can Repair CEP290 mRNA
by
Dooley, Scott J.
,
McDougald, Devin S.
,
Fisher, Krishna J.
,
Bennicelli, Jeanette L.
,
Mitchell, Lloyd G.
,
Bennett, Jean
Published in
Molecular therapy. Nucleic acids
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AAV-mediated PEX1 gene augmentation improves visual function in the PEX1-Gly844Asp mouse model for mild Zellweger spectrum disorder
by
Argyriou, Catherine
,
Polosa, Anna
,
Song, Ji Yun
,
Omri, Samy
,
Steele, Bradford
,
Cécyre, Bruno
,
McDougald, Devin S.
,
Di Pietro, Erminia
,
Bouchard, Jean-François
,
Bennett, Jean
,
Hacia, Joseph G.
,
Lachapelle, Pierre
,
Braverman, Nancy E.
Published in
Molecular therapy. Methods & clinical development
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CRISPR Activation Enhances In Vitro Potency of AAV Vectors Driven by Tissue-Specific Promoters
by
McDougald, Devin S.
,
Duong, Thu T.
,
Palozola, Katherine C.
,
Marsh, Anson
,
Papp, Tyler E.
,
Mills, Jason A.
,
Zhou, Shangzhen
,
Bennett, Jean
Published in
Molecular therapy. Methods & clinical development
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Rescue of retinal ganglion cells in optic nerve injury using cell-selective AAV mediated delivery of SIRT1
by
Ross, Ahmara G
,
McDougald, Devin S
,
Khan, Reas S
,
Duong, Thu T
,
Dine, Kimberly E
,
Aravand, Puya
,
Bennett, Jean
,
Chavali, Venkata Ramana Murthy
,
Shindler, Kenneth S
Published in
Gene therapy
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AKT3 Gene Transfer Promotes Anabolic Reprogramming and Photoreceptor Neuroprotection in a Pre-clinical Model of Retinitis Pigmentosa
by
McDougald, Devin S.
,
Papp, Tyler E.
,
Zezulin, Alexandra U.
,
Zhou, Shangzhen
,
Bennett, Jean
Published in
Molecular therapy
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Dual SMAD inhibition and Wnt inhibition enable efficient and reproducible differentiations of induced pluripotent stem cells into retinal ganglion cells
by
Chavali, Venkata R M
,
Haider, Naqi
,
Rathi, Sonika
,
Vrathasha, Vrathasha
,
Alapati, Teja
,
He, Jie
,
Gill, Kamaljot
,
Nikonov, Roman
,
Duong, Thu T
,
McDougald, Devin S
,
Nikonov, Sergei
,
O'Brien, Joan
,
Mills, Jason A
Published in
Scientific reports
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Personalized models reveal mechanistic and therapeutic insights into CEP290-associated Leber congenital amaurosis
by
McDougald, Devin S
,
Kmiec, Eric
,
Mills, Jason A
Published in
Stem cell investigation
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