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7by Elstein, Deborah, Belmatoug, Nadia, Deegan, Patrick, Göker-Alpan, Özlem, Hughes, Derralynn A, Schwartz, Ida Vanessa D, Weinreb, Neal, Bonner, Nicola, Panter, Charlotte, Fountain, Donna, Lenny, Andrew, Longworth, Louise, Miller, Rachael, Shah, Koonal, Schenk, Jörn, Sen, Rohini, Zimran, AriGet full text
Published in Orphanet journal of rare diseases
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9by Donald, Aimee, Cizer, Huseyin, Finnegan, Niamh, Collin-Histed, Tanya, Hughes, Derralynn A, Davies, Elin HafGet full text
Published in Orphanet journal of rare diseases
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10by Young-Gqamana, Brandy, Brignol, Nastry, Chang, Hui-Hwa, Khanna, Richie, Soska, Rebecca, Fuller, Maria, Sitaraman, Sheela A, Germain, Dominique P, Giugliani, Roberto, Hughes, Derralynn A, Mehta, Atul, Nicholls, Kathy, Boudes, Pol, Lockhart, David J, Valenzano, Kenneth J, Benjamin, Elfrida RGet full text
Published in PloS one
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12by Hughes, Derralynn A, Aguiar, Patricio, Deegan, Patrick B, Ezgu, Fatih, Frustaci, Andrea, Lidove, Olivier, Linhart, Aleš, Lubanda, Jean-Claude, Moon, James C, Nicholls, Kathleen, Niu, Dau-Ming, Nowak, Albina, Ramaswami, Uma, Reisin, Ricardo, Rozenfeld, Paula, Schiffmann, Raphael, Svarstad, Einar, Thomas, Mark, Torra, Roser, Vujkovac, Bojan, Warnock, David G, West, Michael L, Johnson, Jack, Rolfe, Mark J, Feriozzi, SandroGet full text
Published in BMJ open
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13by Schiffmann, Raphael, Bichet, Daniel G, Jovanovic, Ana, Hughes, Derralynn A, Giugliani, Roberto, Feldt-Rasmussen, Ulla, Shankar, Suma P, Barisoni, Laura, Colvin, Robert B, Jennette, J Charles, Holdbrook, Fred, Mulberg, Andrew, Castelli, Jeffrey P, Skuban, Nina, Barth, Jay A, Nicholls, KathleenGet full text
Published in Orphanet journal of rare diseases
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18by Vijapurapu, Ravi, Kozor, Rebecca, Hughes, Derralynn A, Woolfson, Peter, Jovanovic, Ana, Deegan, Patrick, Rusk, Rosemary, Figtree, Gemma A, Tchan, Michel, Whalley, David, Kotecha, Dipak, Leyva, Francisco, Moon, James, Geberhiwot, Tarekegn, Steeds, Richard PGet full text
Published in Current controlled trials in cardiovascular medicine
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19by Bichet, Daniel G., Hopkin, Robert J., Aguiar, Patrício, Allam, Sridhar R., Chien, Yin-Hsiu, Giugliani, Roberto, Kallish, Staci, Kineen, Sabina, Lidove, Olivier, Niu, Dau-Ming, Olivotto, Iacopo, Politei, Juan, Rakoski, Paul, Torra, Roser, Tøndel, Camilla, Hughes, Derralynn A.Get full text
Published in Frontiers in medicine
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