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Search Results - Fraschini, Maddalena
Search Results - Fraschini, Maddalena
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P005: Atidarsagene autotemcel (hematopoietic stem cell–gene therapy) preserves cognitive and motor development in metachromatic leukodystrophy with up to 12 years follow-up
by
Fumagalli, Francesca
,
Calbi, Valeria
,
De Mattia, Fabiola
,
Zambon, Alberto
,
Gallo, Vera
,
Recupero, Salvatore
,
Fratini, Elena Sophia
,
Ippolito, Alessia
,
Ciotti, Francesca
,
Fraschini, Maddalena
,
Sarzana, Marina
,
Scarparo, Stefano
,
Montini, Eugenio
,
Locatelli, Sara
,
Facchini, Marcella
,
Clerici, Alessandra
,
Morena, Francesco
,
Martino, Sabata
,
Yarzi, Muska
,
Moro, Sean
,
Shenker, Andrew
,
Brooks, Jean
,
Richardson, Alan
,
Meltzer, Leslie
,
Campbell, Laura
,
Aiuti, Alessandro
Published in
Genetics in Medicine Open
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Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded acc...
by
Fumagalli, Francesca
,
Calbi, Valeria
,
Natali Sora, Maria Grazia
,
Sessa, Maria
,
Baldoli, Cristina
,
Rancoita, Paola Maria V
,
Ciotti, Francesca
,
Sarzana, Marina
,
Fraschini, Maddalena
,
Zambon, Alberto Andrea
,
Acquati, Serena
,
Redaelli, Daniela
,
Attanasio, Vanessa
,
Miglietta, Simona
,
De Mattia, Fabiola
,
Barzaghi, Federica
,
Ferrua, Francesca
,
Migliavacca, Maddalena
,
Tucci, Francesca
,
Gallo, Vera
,
Del Carro, Ubaldo
,
Canale, Sabrina
,
Spiga, Ivana
,
Lorioli, Laura
,
Recupero, Salvatore
,
Fratini, Elena Sophia
,
Morena, Francesco
,
Silvani, Paolo
,
Calvi, Maria Rosa
,
Facchini, Marcella
,
Locatelli, Sara
,
Corti, Ambra
,
Zancan, Stefano
,
Antonioli, Gigliola
,
Farinelli, Giada
,
Gabaldo, Michela
,
Garcia-Segovia, Jesus
,
Schwab, Laetitia C
,
Downey, Gerald F
,
Filippi, Massimo
,
Cicalese, Maria Pia
,
Martino, Sabata
,
Di Serio, Clelia
,
Ciceri, Fabio
,
Bernardo, Maria Ester
,
Naldini, Luigi
,
Biffi, Alessandra
,
Aiuti, Alessandro
Published in
The Lancet (British edition)
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Lentiviral hematopoietic stem cell gene therapy (atidarsagene autotemcel) for late juvenile metachromatic leukodystrophy (MLD)
by
Gallo, Vera
,
Calbi, Valeria
,
De Mattia, Fabiola
,
Zambon, Alberto Andrea
,
Recupero, Salvatore
,
Fratini, Elena Sophia
,
Ciotti, Francesca
,
Fraschini, Maddalena
,
Sangalli, Mara
,
Sarzana, Marina
,
Clerici, Alessandra
,
Morena, Francesco
,
Martino, Sabata
,
Brooks, Jean
,
Richardson, Alan
,
Campbell, Laura
,
Aiuti, Alessandro
,
Fumagalli, Francesca
Published in
Molecular genetics and metabolism
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Atidarsagene autotemcel (autologous hematopoietic stem cell gene therapy) preserves cognitive and motor development in early-onset metachromatic leukodystrophy with up to 12 years...
by
Fumagalli, Francesca
,
Calbi, Valeria
,
De Mattia, Fabiola
,
Zambon, Alberto Andrea
,
Gallo, Vera
,
Recupero, Salvatore
,
Fratini, Elena Sophia
,
Ippolito, Alessia
,
Ciotti, Francesca
,
Fraschini, Maddalena
,
Sarzana, Marina
,
Scarparo, Stefano
,
Montini, Eugenio
,
Locatelli, Sara
,
Facchini, Marcella
,
Clerici, Alessandra
,
Morena, Francesco
,
Martino, Sabata
,
Yarzi, Muska
,
Moro, Sean
,
Shenker, Andrew
,
Brooks, Jean
,
Richardson, Alan
,
Campbell, Laura
,
Aiuti, Alessandro
Published in
Molecular genetics and metabolism
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Long-term clinical outcomes of atidarsagene autotemcel (autologous hematopoietic stem cell gene therapy [HSC-GT] for metachromatic leukodystrophy) with up to 11 years follow-up
by
Fumagalli, Francesca
,
Calbi, Valeria
,
De Mattia, Fabiola
,
Zambon, Alberto A.
,
Gallo, Vera
,
Recupero, Salvatore
,
Baldoli, Cristina
,
Fratini, Elena Sophia
,
Ciotti, Francesca
,
Fraschini, Maddalena
,
Sarzana, Marina
,
Scarparo, Stefano
,
Calabria, Andrea
,
Montini, Eugenio
,
Locatelli, Sara
,
Facchini, Marcella
,
Clerici, Alessandra
,
Morena, Francesco
,
Martino, Sabata
,
Claros, Angelica
,
Kaviya, Arpeat
,
Moro, Sean
,
Brooks, Jean
,
Richardson, Alan
,
Aiuti, Alessandro
Published in
Molecular genetics and metabolism
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Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in 5 patients treated under nominal compassionate use
by
Calbi, Valeria
,
Fumagalli, Francesca
,
Gallo, Vera
,
Recupero, Salvatore
,
De Mattia, Fabiola
,
Fratini, Elena Sophia
,
Corti, Ambra
,
Tarantola, Giulia
,
Sarzana, Marina
,
Ippolito, Alessia
,
Scarparo, Stefano
,
Ciotti, Francesca
,
Fraschini, Maddalena
,
Levi, Margherita
,
Sangalli, Mara
,
Morena, Francesco
,
Martino, Sabata
,
Sevin, Caroline
,
Narayanan, Vinodh
,
Adam, Etai
,
Emrick, Lisa
,
Giugliani, Roberto
,
Aiuti, Alessandro
Published in
Molecular genetics and metabolism
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Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in nine patients treated with a cryopreserved formulation of OTL-200
by
Calbi, Valeria
,
Fumagalli, Francesca
,
De Mattia, Fabiola
,
Fratini, Elena
,
Ferrua, Francesca
,
Barzaghi, Federica
,
Cicalese, Maria Pia
,
Migliavacca, Maddalena
,
Tucci, Francesca
,
Gallo, Vera
,
Ciotti, Francesca
,
Fraschini, Maddalena
,
Sarzana, Marina
,
Locatelli, Sara
,
Sangalli, Mara
,
Morena, Francesco
,
Segovia, Jesus
,
Schwab, Laetitia C.
,
Downey, Gerald
,
Martino, Sabata
,
Ciceri, Fabio
,
Bernardo, Maria Ester
,
Naldini, Luigi
,
Aiuti, Alessandro
Published in
Molecular genetics and metabolism
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