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RICTOR/mTORC2 downregulation in BRAFV600E melanoma cells promotes resistance to BRAF/MEK inhibition
by
Ponzone, Luca
,
Audrito, Valentina
,
Landi, Claudia
,
Moiso, Enrico
,
Levra Levron, Chiara
,
Ferrua, Sara
,
Savino, Aurora
,
Vitale, Nicoletta
,
Gasparrini, Massimiliano
,
Avalle, Lidia
,
Vantaggiato, Lorenza
,
Shaba, Enxhi
,
Tassone, Beatrice
,
Saoncella, Stefania
,
Orso, Francesca
,
Viavattene, Daniele
,
Marina, Eleonora
,
Fiorilla, Irene
,
Burrone, Giulia
,
Abili, Youssef
,
Altruda, Fiorella
,
Bini, Luca
,
Deaglio, Silvia
,
Defilippi, Paola
,
Menga, Alessio
,
Poli, Valeria
,
Porporato, Paolo Ettore
,
Provero, Paolo
,
Raffaelli, Nadia
,
Riganti, Chiara
,
Taverna, Daniela
,
Cavallo, Federica
,
Calautti, Enzo
Published in
Molecular cancer
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RICTOR/mTORC2 downregulation in BRAF V600E melanoma cells promotes resistance to BRAF/MEK inhibition
by
Ponzone, Luca
,
Audrito, Valentina
,
Landi, Claudia
,
Moiso, Enrico
,
Levra Levron, Chiara
,
Ferrua, Sara
,
Savino, Aurora
,
Vitale, Nicoletta
,
Gasparrini, Massimiliano
,
Avalle, Lidia
,
Vantaggiato, Lorenza
,
Shaba, Enxhi
,
Tassone, Beatrice
,
Saoncella, Stefania
,
Orso, Francesca
,
Viavattene, Daniele
,
Marina, Eleonora
,
Fiorilla, Irene
,
Burrone, Giulia
,
Abili, Youssef
,
Altruda, Fiorella
,
Bini, Luca
,
Deaglio, Silvia
,
Defilippi, Paola
,
Menga, Alessio
,
Poli, Valeria
,
Porporato, Paolo Ettore
,
Provero, Paolo
,
Raffaelli, Nadia
,
Riganti, Chiara
,
Taverna, Daniela
,
Cavallo, Federica
,
Calautti, Enzo
Published in
Molecular cancer
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Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
by
Aiuti, Alessandro
,
Biasco, Luca
,
Scaramuzza, Samantha
,
Ferrua, Francesca
,
Cicalese, Maria Pia
,
Baricordi, Cristina
,
Dionisio, Francesca
,
Calabria, Andrea
,
Giannelli, Stefania
,
Castiello, Maria Carmina
,
Bosticardo, Marita
,
Evangelio, Costanza
,
Assanelli, Andrea
,
Casiraghi, Miriam
,
Di Nunzio, Sara
,
Callegaro, Luciano
,
Benati, Claudia
,
Rizzardi, Paolo
,
Pellin, Danilo
,
Di Serio, Clelia
,
Schmidt, Manfred
,
Von Kalle, Christof
,
Gardner, Jason
,
Mehta, Nalini
,
Neduva, Victor
,
Dow, David J.
,
Galy, Anne
,
Miniero, Roberto
,
Finocchi, Andrea
,
Metin, Ayse
,
Banerjee, Pinaki P.
,
Orange, Jordan S.
,
Galimberti, Stefania
,
Valsecchi, Maria Grazia
,
Biffi, Alessandra
,
Montini, Eugenio
,
Villa, Anna
,
Ciceri, Fabio
,
Roncarolo, Maria Grazia
,
Naldini, Luigi
Published in
Science (American Association for the Advancement of Science)
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Lentiviral haematopoietic stem-cell gene therapy for early-onset metachromatic leukodystrophy: long-term results from a non-randomised, open-label, phase 1/2 trial and expanded acc...
by
Fumagalli, Francesca
,
Calbi, Valeria
,
Natali Sora, Maria Grazia
,
Sessa, Maria
,
Baldoli, Cristina
,
Rancoita, Paola Maria V
,
Ciotti, Francesca
,
Sarzana, Marina
,
Fraschini, Maddalena
,
Zambon, Alberto Andrea
,
Acquati, Serena
,
Redaelli, Daniela
,
Attanasio, Vanessa
,
Miglietta, Simona
,
De Mattia, Fabiola
,
Barzaghi, Federica
,
Ferrua, Francesca
,
Migliavacca, Maddalena
,
Tucci, Francesca
,
Gallo, Vera
,
Del Carro, Ubaldo
,
Canale, Sabrina
,
Spiga, Ivana
,
Lorioli, Laura
,
Recupero, Salvatore
,
Fratini, Elena Sophia
,
Morena, Francesco
,
Silvani, Paolo
,
Calvi, Maria Rosa
,
Facchini, Marcella
,
Locatelli, Sara
,
Corti, Ambra
,
Zancan, Stefano
,
Antonioli, Gigliola
,
Farinelli, Giada
,
Gabaldo, Michela
,
Garcia-Segovia, Jesus
,
Schwab, Laetitia C
,
Downey, Gerald F
,
Filippi, Massimo
,
Cicalese, Maria Pia
,
Martino, Sabata
,
Di Serio, Clelia
,
Ciceri, Fabio
,
Bernardo, Maria Ester
,
Naldini, Luigi
,
Biffi, Alessandra
,
Aiuti, Alessandro
Published in
The Lancet (British edition)
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Wiskott-Aldrich syndrome: a study of 577 patients defines the genotype as a biomarker for disease severity and survival
by
Vallée, Tanja C.
,
Glasmacher, Jannik S.
,
Buchner, Hannes
,
Arkwright, Peter D.
,
Behrends, Uta
,
Bondarenko, Anastasia
,
Browning, Michael J.
,
Buchbinder, David
,
Cattoni, Alessandro
,
Chernyshova, Liudmyla
,
Ciznar, Peter
,
Cole, Theresa
,
Czogała, Wojciech
,
Dueckers, Gregor
,
Edgar, John David M.
,
Erbey, Fatih
,
Fasth, Anders
,
Ferrua, Francesca
,
Formankova, Renata
,
Gambineri, Eleonora
,
Gennery, Andrew R.
,
Goldman, Frederick D.
,
Gonzalez-Granado, Luis I.
,
Heilmann, Carsten
,
Heiskanen-Kosma, Tarja
,
Juntti, Hanna
,
Kainulainen, Leena
,
Kanegane, Hirokazu
,
Karaca, Neslihan E.
,
Kilic, Sara S.
,
Klein, Christoph
,
Kołtan, Sylwia
,
Kondratenko, Irina
,
Meyts, Isabelle
,
Nasrullayeva, Gulnara M.
,
Notarangelo, Lucia D.
,
Pasic, Srdjan
,
Pellier, Isabelle
,
Pignata, Claudio
,
Misbah, Siraj
,
Schulz, Ansgar
,
Segundo, Gesmar R.
,
Shcherbina, Anna
,
Slatter, Mary
,
Sokolic, Robert
,
Soler-Palacin, Pere
,
Stepensky, Polina
,
van Montfrans, Joris M.
,
Ryhänen, Samppa
,
Wolska-Kuśnierz, Beata
,
Ziegler, John B.
,
Zhao, Xiaodong
,
Aiuti, Alessandro
,
Ochs, Hans D.
,
Albert, Michael H.
Published in
Blood
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Mild SARS-CoV-2 Infection After Gene Therapy in a Child With Wiskott-Aldrich Syndrome: A Case Report
by
Cenciarelli, Sabina
,
Calbi, Valeria
,
Barzaghi, Federica
,
Bernardo, Maria Ester
,
Oltolini, Chiara
,
Migliavacca, Maddalena
,
Gallo, Vera
,
Tucci, Francesca
,
Fraschetta, Federico
,
Albertazzi, Elena
,
Fratini, Elena Sophia
,
Consiglieri, Giulia
,
Giannelli, Stefania
,
Dionisio, Francesca
,
Sartirana, Claudia
,
Racca, Sara
,
Camesasca, Chiara
,
Peretto, Giovanni
,
Daverio, Rita
,
Esposito, Antonio
,
De Cobelli, Francesco
,
Silvani, Paolo
,
Rabusin, Marco
,
Cara, Andrea
,
Trabattoni, Daria
,
Dispinseri, Stefania
,
Scarlatti, Gabriella
,
Piemonti, Lorenzo
,
Lampasona, Vito
,
Cicalese, Maria Pia
,
Aiuti, Alessandro
,
Ferrua, Francesca
Published in
Frontiers in immunology
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Wiskott-Aldrich Syndrome: A study on 577 patients defining the genotype as a predictive biomarker for disease severity
by
Vallée, Tanja C
,
Glasmacher, Jannik S
,
Buchner, Hannes
,
Arkwright, Peter D
,
Behrends, Uta
,
Bondarenko, Anastasia
,
Browning, Michael J
,
Buchbinder, David K
,
Cattoni, Alessandro
,
Chernyshova, Liudmyla
,
Ciznar, Peter
,
Cole, Theresa
,
Czogala, Wojciech
,
Dueckers, Gregor
,
Edgar, John David M
,
Erbey, Fatih
,
Fasth, Anders
,
Ferrua, Francesca
,
Formankova, Renata
,
Gambineri, Eleonora
,
Gennery, Andrew R
,
Goldman, Frederick D
,
Gonzalez-Granado, Luis Ignacio
,
Heilmann, Carsten
,
Heiskanen-Kosma, Tarja
,
Juntti, Hanna
,
Kainulainen, Leena
,
Kanegane, Hirokazu
,
Karaca, Neslihan E
,
Kilic, Sara S
,
Klein, Christoph
,
Koltan, MD, PhD, Sylwia
,
Kondratenko, Irina
,
Meyts, Isabelle
,
Nasrullayeva, Gulnara M
,
Notarangelo, Lucia Dora
,
Pasic, Srdjan
,
Pellier, Isabelle
,
Pignata, Claudio
,
Misbah, Siraj Ahmed
,
Schulz, Ansgar S
,
Segundo, Gesmar Rs
,
Shcherbina, Anna
,
Slatter, Mary A
,
Sokolic, Robert
,
Soler-Palacin, Pere
,
Stepensky, Polina
,
van Montfrans, Joris M
,
Ryhänen, Samppa
,
Wolska-Kuśnierz, MD, PhD, Beata
,
Ziegler, John B
,
Zhao, Xiaodong
,
Aiuti, Alessandro
,
Ochs, Hans D
,
Albert, Michael H
Published in
Blood
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Lentiviral haematopoietic stem cell gene therapy for metachromatic leukodystrophy: Results in nine patients treated with a cryopreserved formulation of OTL-200
by
Calbi, Valeria
,
Fumagalli, Francesca
,
De Mattia, Fabiola
,
Fratini, Elena
,
Ferrua, Francesca
,
Barzaghi, Federica
,
Cicalese, Maria Pia
,
Migliavacca, Maddalena
,
Tucci, Francesca
,
Gallo, Vera
,
Ciotti, Francesca
,
Fraschini, Maddalena
,
Sarzana, Marina
,
Locatelli, Sara
,
Sangalli, Mara
,
Morena, Francesco
,
Segovia, Jesus
,
Schwab, Laetitia C.
,
Downey, Gerald
,
Martino, Sabata
,
Ciceri, Fabio
,
Bernardo, Maria Ester
,
Naldini, Luigi
,
Aiuti, Alessandro
Published in
Molecular genetics and metabolism
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Absence of VOD in paediatric thalassaemic HSCT recipients using defibrotide prophylaxis and intravenous Busulphan
by
Cappelli, Barbara
,
Chiesa, Robert
,
Evangelio, Costanza
,
Biffi, Alessandra
,
Roccia, Tito
,
Frugnoli, Ilaria
,
Biral, Erika
,
Noè, Anna
,
Fossati, Marco
,
Finizio, Valentina
,
Miniero, Roberto
,
Napolitano, Sara
,
Ferrua, Francesca
,
Soliman, Clara
,
Ciceri, Fabio
,
Roncarolo, Maria G.
,
Marktel, Sarah
Published in
British journal of haematology
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Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
by
Aiuti, Alessandro
,
Biasco, Luca
,
Scaramuzza, Samantha
,
Ferrua, Francesca
,
Cicalese, Maria Pia
,
Baricordi, Cristina
,
Dionisio, Francesca
,
Calabria, Andrea
,
Giannelli, Stefania
,
Castiello, Maria Carmina
,
Bosticardo, Marita
,
Evangelio, Costanza
,
Assanelli, Andrea
,
Casiraghi, Miriam
,
Di Nunzio, Sara
,
Callegaro, Luciano
,
Benati, Claudia
,
Rizzardi, Paolo
,
Pellin, Danilo
,
Di Serio, Clelia
,
Schmidt, Manfred
,
von Kalle, Christof
,
Gardner, Jason
,
Mehta, Nalini
,
Neduva, Victor
,
Dow, David
,
Galy, Anne
,
Miniero, Roberto
,
Finocchi, Andrea
,
Metin, Ayse
,
Banerjee, Pinaki
,
Orange, Jordan
,
Galimberti, Stefania
,
Valsecchi, Maria Grazia
,
Biffi, Alessandra
,
Montini, Eugenio
,
Villa, Anna
,
Ciceri, Fabio
,
Roncarolo, Maria Grazia
,
Naldini, Luigi
Published in
Science (American Association for the Advancement of Science)
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Lentivirus-based Gene Therapy of Hematopoietic Stem Cells in Wiskott-Aldrich Syndrome
by
Aiuti, Alessandro
,
Biasco, Luca
,
Scaramuzza, Samantha
,
Ferrua, Francesca
,
Cicalese, Maria Pia
,
Baricordi, Cristina
,
Dionisio, Francesca
,
Calabria, Andrea
,
Giannelli, Stefania
,
Castiello, Maria Carmina
,
Bosticardo, Marita
,
Evangelio, Costanza
,
Assanelli, Andrea
,
Casiraghi, Miriam
,
Di Nunzio, Sara
,
Callegaro, Luciano
,
Benati, Claudia
,
Rizzardi, Paolo
,
Pellin, Danilo
,
Di Serio, Clelia
,
Schmidt, Manfred
,
Von Kalle, Christof
,
Gardner, Jason
,
Mehta, Nalini
,
Neduva, Victor
,
Dow, David J.
,
Galy, Anne
,
Miniero, Roberto
,
Finocchi, Andrea
,
Metin, Ayse
,
Banerjee, Pinaki
,
Orange, Jordan
,
Galimberti, Stefania
,
Valsecchi, Maria Grazia
,
Biffi, Alessandra
,
Montini, Eugenio
,
Villa, Anna
,
Ciceri, Fabio
,
Roncarolo, Maria Grazia
,
Naldini, Luigi
Published in
Science (American Association for the Advancement of Science)
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Mild SARS-CoV-2 Infection After Gene Therapy in a Child With Wiskott-Aldrich Syndrome: A Case Report
by
Cenciarelli, Sabina
,
Calbi, Valeria
,
Barzaghi, Federica
,
Bernardo, Maria Ester
,
Oltolini, Chiara
,
Migliavacca, Maddalena
,
Gallo, Vera
,
Tucci, Francesca
,
Fraschetta, Federico
,
Albertazzi, Elena
,
Fratini, Elena Sophia
,
Consiglieri, Giulia
,
Giannelli, Stefania
,
Dionisio, Francesca
,
Sartirana, Claudia
,
Racca, Sara
,
Camesasca, Chiara
,
Peretto, Giovanni
,
Daverio, Rita
,
Esposito, Antonio
,
De Cobelli, Francesco
,
Silvani, Paolo
,
Rabusin, Marco
,
Cara, Andrea
,
Trabattoni, Daria
,
Dispinseri, Stefania
,
Scarlatti, Gabriella
,
Piemonti, Lorenzo
,
Lampasona, Vito
,
Cicalese, Maria Pia
,
Aiuti, Alessandro
,
Ferrua, Francesca
Published in
Frontiers in immunology
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