Brain and visceral gene editing of mucopolysaccharidosis I mice by nasal delivery of the CRISPR/Cas9 system by Vera, Luisa Natalia Pimentel, Schuh, Roselena Silvestri, Fachel, Flavia Nathielly Silveira, Poletto, Edina, Piovesan, Eduarda, Kubaski, Francyne, Couto, Eduarda, Brum, Bruna, Rodrigues, Graziella, Souza, Hallana, Giugliani, Roberto, Matte, Ursula, Baldo, Guilherme, Teixeira, Helder F.

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