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Search Results - Cwerman-Thibault, Hélène
Search Results - Cwerman-Thibault, Hélène
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Nuclear expression of mitochondrial ND4 leads to the protein assembling in complex I and prevents optic atrophy and visual loss
by
Cwerman-Thibault, Hélène
,
Augustin, Sébastien
,
Lechauve, Christophe
,
Ayache, Jessica
,
Ellouze, Sami
,
Sahel, José-Alain
,
Corral-Debrinski, Marisol
Published in
Molecular therapy
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Neuroglobin effectively halts vision loss in Harlequin mice at an advanced stage of optic nerve degeneration
by
Cwerman-Thibault, Hélène
,
Lechauve, Christophe
,
Malko-Baverel, Vassilissa
,
Augustin, Sébastien
,
Le Guilloux, Gwendoline
,
Reboussin, Élodie
,
Degardin-Chicaud, Julie
,
Simonutti, Manuel
,
Debeir, Thomas
,
Corral-Debrinski, Marisol
Published in
Neurobiology of disease
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Mitochondrial medicine: to a new era of gene therapy for mitochondrial DNA mutations
by
Cwerman-Thibault, Hélène
,
Sahel, José-Alain
,
Corral-Debrinski, Marisol
Published in
Journal of inherited metabolic disease
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Harlequin mice exhibit cognitive impairment, severe loss of Purkinje cells and a compromised bioenergetic status due to the absence of Apoptosis Inducing Factor
by
Cwerman-Thibault, Hélène
,
Malko-Baverel, Vassilissa
,
Le Guilloux, Gwendoline
,
Torres-Cuevas, Isabel
,
Ratcliffe, Edward
,
Mouri, Djmila
,
Mignon, Virginie
,
Saubaméa, Bruno
,
Boespflug-Tanguy, Odile
,
Gressens, Pierre
,
Corral-Debrinski, Marisol
Published in
Biochimica et biophysica acta. Molecular basis of disease
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Neuroglobin involvement in respiratory chain function and retinal ganglion cell integrity
by
Lechauve, Christophe
,
Augustin, Sébastien
,
Cwerman-Thibault, Hélène
,
Bouaita, Aïcha
,
Forster, Valérie
,
Célier, Chantal
,
Rustin, Pierre
,
Marden, Michael C.
,
Sahel, José-Alain
,
Corral-Debrinski, Marisol
Published in
Biochimica et biophysica acta. Molecular cell research
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Neuroglobin Gene Therapy Prevents Optic Atrophy and Preserves Durably Visual Function in Harlequin Mice
by
Lechauve, Christophe
,
Augustin, Sébastien
,
Cwerman-Thibault, Hélène
,
Reboussin, Élodie
,
Roussel, Delphine
,
Lai-Kuen, René
,
Saubamea, Bruno
,
Sahel, José-Alain
,
Debeir, Thomas
,
Corral-Debrinski, Marisol
Published in
Molecular therapy
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Downregulation of apoptosis-inducing factor in Harlequin mice induces progressive and severe optic atrophy which is durably prevented by AAV2-AIF1 gene therapy
by
Bouaita, Aicha
,
Augustin, Sébastien
,
Lechauve, Christophe
,
Cwerman-Thibault, Hélène
,
Bénit, Paule
,
Simonutti, Manuel
,
Paques, Michel
,
Rustin, Pierre
,
Sahel, José-Alain
,
Corral-Debrinski, Marisol
Published in
Brain (London, England : 1878)
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Neuroglobin Can Prevent or Reverse Glaucomatous Progression in DBA/2J Mice
by
Cwerman-Thibault, Hélène
,
Lechauve, Christophe
,
Augustin, Sébastien
,
Roussel, Delphine
,
Reboussin, Élodie
,
Mohammad, Ammara
,
Degardin-Chicaud, Julie
,
Simonutti, Manuel
,
Liang, Hong
,
Brignole-Baudouin, Françoise
,
Maron, Anne
,
Debeir, Thomas
,
Corral-Debrinski, Marisol
Published in
Molecular therapy. Methods & clinical development
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Gene therapy for mitochondrial diseases: Leber Hereditary Optic Neuropathy as the first candidate for a clinical trial
by
Cwerman-Thibault, Hélène
,
Augustin, Sébastien
,
Ellouze, Sami
,
Sahel, José-Alain
,
Corral-Debrinski, Marisol
Published in
Comptes rendus. Biologies
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Mitochondrial medicine: to a new era of gene therapy for mitochondrial DNA mutations : MITOCHONDRIAL MEDICINE
by
CWERMAN-THIBAULT, Hélène
,
SAHEL, José-Alain
,
CORRAL-DEBRINSKI, Marisol
Published in
Journal of inherited metabolic disease
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Journal Of Inherited Metabolic Disease
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Molecular Therapy
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Retinal Ganglion Cells
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