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Recombinant FVIIIFc-VWF-XTEN Demonstrates Significant Bioavailability Following Subcutaneous Administration in Hemophilia A Mice
by
Drager, Douglas
,
Patarroyo-White, Sue
,
Chao, Hoson
,
Ismail, Ayman
,
Liu, Jiayun
,
Holthaus, Amy M
,
Chhabra, Ekta
,
Kulman, John
,
Schellenberger, Volker
,
Liu, Tongyao
,
Peters, Robert
Published in
Blood
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Comparative Studies Reveal Robust HbF Induction By Editing of HBG1/2 Promoters or BCL11A Erythroid-Enhancer in Human CD34+ Cells but That BCL11A Erythroid-Enhancer Editing Is Assoc...
by
Chang, Kai-Hsin
,
Sanchez, Minerva
,
Heath, Jack
,
deDreuzy, Edouard
,
Haskett, Scott
,
Vogelaar, Abigail
,
Gogi, Kiran
,
Da Silva, Jen
,
Wang, Tongyao
,
Sadowski, Andrew
,
Gotta, Gregory
,
Siwak, Jamaica
,
Viswanathan, Ramya
,
Loveluck, Katherine
,
Chao, Hoson
,
Tillotson, Eric
,
Chalishazar, Aditi
,
Dass, Abhishek
,
Ta, Frederick
,
Brennan, Emily
,
Tabbaa, Diana
,
Marco, Eugenio
,
Zuris, John A
,
Reyon, Deepak
,
Isik, Meltem
,
Friedland, Ari
,
Ta, Terence
,
Harbinski, Fred
,
Giannoukos, Georgia
,
Teixeira, Sandra
,
Wilson, Christopher J
,
Albright, Charlie
,
Jiang, Haiyan
Published in
Blood
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