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Tissue-specific activation of gene expression by the Synergistic Activation Mediator (SAM) CRISPRa system in mice
by
Hunt, Charleen
,
Hartford, Suzanne A
,
White, Derek
,
Pefanis, Evangelos
,
Hanna, Timothy
,
Herman, Clarissa
,
Wiley, Jarrell
,
Brown, Heather
,
Su, Qi
,
Xin, Yurong
,
Voronin, Dennis
,
Nguyen, Hien
,
Altarejos, Judith
,
Crosby, Keith
,
Haines, Jeffery
,
Cancelarich, Sarah
,
Drummond, Meghan
,
Moller-Tank, Sven
,
Malpass, Ryan
,
Buckley, Jacqueline
,
Del Pilar Molina-Portela, Maria
,
Droguett, Gustavo
,
Frendewey, David
,
Chiao, Eric
,
Zambrowicz, Brian
,
Gong, Guochun
Published in
Nature communications
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Recovery kinetics of dual AAV-mediated human otoferlin expression
by
Sellon, Jonathan B
,
So, Kathy S
,
D'Arcangelo, Andrew
,
Cancelarich, Sarah
,
Drummond, Meghan C
,
Slade, Peter G
,
Pan, Ning
,
Gibson, Tyler M
,
Yang, Tian
,
Burns, Joseph C
,
Palermo, Adam T
,
Becker, Lars
Published in
Frontiers in molecular neuroscience
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