Generation of an HIV-1-Resistant Immune System with CD34+ Hematopoietic Stem Cells Transduced with a Triple-Combination Anti-HIV Lentiviral Vector

by WALKER, Jon E, CHEN, Rachel X, MCGEE, Jeannine, NACEY, Catherine, POLLARD, Richard B, ABEDI, Mehrdad, BAUER, Gerhard, NOLTA, Jan A, ANDERSON, Joseph S
Published in Journal of Virology

Allele-Specific Reduction of the Mutant Huntingtin Allele Using Transcription Activator-Like Effectors in Human Huntington's Disease Fibroblasts

by Fink, Kyle D., Deng, Peter, Gutierrez, Josh, Anderson, Joseph S., Torrest, Audrey, Komarla, Anvita, Kalomoiris, Stefanos, Cary, Whitney, Anderson, Johnathon D., Gruenloh, William, Duffy, Alexandra, Tempkin, Teresa, Annett, Geralyn, Wheelock, Vicki, Segal, David J., Nolta, Jan A.
Published in Cell transplantation

A novel Huntington's disease mouse model to assess the role of neuroinflammation on disease progression and to develop human cell therapies

by Dahlenburg, Heather, Cameron, David, Yang, Sheng, Bachman, Angelica, Pollock, Kari, Cary, Whitney, Pham, Missy, Hendrix, Kyle, White, Jeannine, Nelson, Haley, Deng, Peter, Anderson, Joseph S., Fink, Kyle, Nolta, Jan
Published in Stem cells translational medicine

Generation of HIV-1 Resistant and Functional Macrophages From Hematopoietic Stem Cell–derived Induced Pluripotent Stem Cells

by Kambal, Amal, Mitchell, Gaela, Cary, Whitney, Gruenloh, William, Jung, Yunjoon, Kalomoiris, Stefanos, Nacey, Catherine, McGee, Jeannine, Lindsey, Matt, Fury, Brian, Bauer, Gerhard, Nolta, Jan A, Anderson, Joseph S
Published in Molecular therapy

Functional rescue in an Angelman syndrome model following treatment with lentivector transduced hematopoietic stem cells

by Adhikari, Anna, Copping, Nycole A, Beegle, Julie, Cameron, David L, Deng, Peter, O’Geen, Henriette, Segal, David J, Fink, Kyle D, Silverman, Jill L, Anderson, Joseph S
Published in Human molecular genetics

Derivation of normal macrophages from human embryonic stem (hES) cells for applications in HIV gene therapy

by Anderson, Joseph S, Bandi, Sriram, Kaufman, Dan S, Akkina, Ramesh
Published in Retrovirology

Preintegration HIV-1 Inhibition by a Combination Lentiviral Vector Containing a Chimeric TRIM5α Protein, a CCR5 shRNA, and a TAR Decoy

by Anderson, Joseph S, Javien, John, Nolta, Jan A, Bauer, Gerhard
Published in Molecular therapy

Safety and Efficacy of a tCD25 Preselective Combination Anti‐HIV Lentiviral Vector in Human Hematopoietic Stem and Progenitor Cells

by Barclay, Sharlie L., Yang, Yimin, Zhang, Siruo, Fong, Ryan, Barraza, Alfonso, Nolta, Jan A., Torbett, Bruce E., Abedi, Mehrdad, Bauer, Gerhard, Anderson, Joseph S.
Published in Stem cells (Dayton, Ohio)

Roles of Human Parainfluenza Virus Type 3 Bases 13 to 78 in Replication and Transcription: Identification of an Additional Replication Promoter Element and Evidence for Internal Tr...

by HOFFMAN, Michael A, THORSON, Leeanne M, VICKMAN, John E, ANDERSON, Joseph S, MAY, Nathan A, SCHWEITZER, Michelle N
Published in Journal of Virology

Canine Epidermal Neural Crest Stem Cells: Characterization and Potential as Therapy Candidate for a Large Animal Model of Spinal Cord Injury

by Gericota, Barbara, Anderson, Joseph S., Mitchell, Gaela, Borjesson, Dori L., Sturges, Beverly K., Nolta, Jan A., Sieber-Blum, Maya
Published in Stem cells translational medicine

757. Engineered Expression of Novel TRIM5 Isoforms Inhibits HIV-1 Infection in CD34 Hematopoietic Stem Cell Derived Macrophages

by Anderson, Joseph S., Akkina, Ramesh
Published in Molecular therapy

1046. Derivation of Functionally Normal Macrophages from Human Embryonic Stem (hES) Cells for HIV-1 Gene Therapy

by Anderson, Joseph S., Bandi, Sriram, Kaufman, Dan S., Akkina, Ramesh
Published in Molecular therapy

800. Complete Suppression of CCR5 Expression and Inhibition of HIV-1 Infection by Transfected and Lentiviral Vector Expressed shRNAs

by Anderson, Joseph S., Vermeulen, Annaleen, Karpilow, Jon, Akkina, Ramesh
Published in Molecular therapy

296. Pre-Selection of Anti-HIV Lentiviral Vector Gene Modified Hematopoietic Stem Cells Significantly Improves Protection from HIV Infection: The Basis for a Future Clinical Trial

by Barclay, Sharlie L., Yang, Yimin, Zhang, Sirou, Fong, Ryan, Barraza, Alfonso, Nolta, Jan A., Abedi, Mehrdad, Anderson, Joseph S.
Published in Molecular therapy

Preintegration HIV-1 Inhibition by a Combination Lentiviral Vector Containing a Chimeric TRIM5[alpha] Protein, a CCR5 shRNA, and a TAR Decoy

by Anderson, Joseph S, Javien, John, Nolta, Jan A, Bauer, Gerhard
Published in Molecular therapy

The SANAD II study of the effectiveness and cost-effectiveness of valproate versus levetiracetam for newly diagnosed generalised and unclassifiable epilepsy: an open-label, non-inf...

by Burnside, Girvan, Appleton, Richard, Smith, Dave, Leach, John Paul, Sills, Graeme, Tudur-Smith, Catrin, Plumpton, Catrin, Hughes, Dyfrig A, Williamson, Paula, Taylor, Claire, Hindley, Dan, Maguire, Melissa, Smith, Philip E, Lanyon, Karen, Manford, Mark, Parker, Alasdair, Swiderska, Nina, Appleton, Richard, Pauling, James, Hughes, Adrian, Gupta, Rajat, Hanif, Sadia, Awadh, Mostafa, Ragunathan, Sharmini, Cable, Nicola, Cooper, Paul, Hindley, Daniel, Rakshi, Karl, Molloy, Sophie, Ayonrinde, Kunle, Wilson, Martin, Saladi, Satyanarayana, Funston, Lesley-Ann, Cassidy, Damhait, Ratnayaka, Mal, Faza, Hani, Sadler, Martin, Al-Moasseb, Hassan, Galtrey, Clare, Wren, Damien, Olabi, Anas, Khan, Muhammed, Kallappa, Chetana, Chinthapalli, Ravi, Hitiris, Nikolas, Maguire, Melissa, Hussain, Nahin, Dowson, Simon, Ellison, Julie, Sharrack, Basil, Gandhi, Vandna, Tittensor, Phil, Summers, Beatrice, Shashikiran, Sastry, Dison, Penelope J, Samarasekera, Shanika, McCorry, Doug, White, Kathleen, Nithi, Kannan, Richardson, Martin, Brown, Richard, Deekollu, David, Slaght, Sean, Ahmed, Mansoor, Chaudhuri, Abhijit, Chow, Gabriel, Artal, Javier, Kucinskiene, Danute, Sreenivasa, Harish, Velmurugan, Singara, Zipitis, Christos S, McLean, Brendan, Gregoriou, Angelous, Maddison, Paul, Lawthom, Charlotte, Kinton, Lucy, Kelso, Andrew, Hughes, Imelda, Martland, John, Emsley, Hedley, de Goede, Christian, Moor, Carl-Christian, Aram, Julia, Mohanraj, Rajiv, Nelapatla, Suresh, Rittey, Chris, Cock, Hannah, Richardson, Anna, Houston, Erika, Lawson, Geoff, Burness, Christine, Wieshmann, Udo, Dey, Indranil, Sivakumar, Puthuval, Yeung, Lap-Kong, Smith, Philip, Heafield, Tom, Mathew, Anna, Smith, David, Jauhari, Praveen
Published in The Lancet (British edition)

Hallmarks of HIV-1 pathogenesis are modulated by Nef's Secretion Modification Region

by Konadu, Kateena Addae, Anderson, Joseph S, Huang, Ming-Bo, Ali, Syed A, Powell, Michael D, Villinger, Francois, Bond, Vincent C
Published in Journal of AIDS & clinical research

Generation of HIV Resistant and Functional Macrophages From Hematopoietic Stem Cell Derived Induced Pluripotent Stem Cells

by Kambal, Amal, Mitchell, Gaela, Cary, Whitney, Gruenloh, William, Jung, Yunjoon, Nacey, Catherine, Kalomoiris, Stefanos, Lindsey, Matt, Bauer, Gerhard, Nolta, Jan A., Anderson, Joseph S.
Published in Blood

Evaluating the Safety and Efficacy of Anti-HIV Transgenic Cells in a Humanized Mouse Model (NOD/SCIDγc−/−) for HIV Stem Cell Gene Therapy

by Anderson, Joseph S., Walker, Jon, Wirthlin, Louisa, Javien, John, Nolta, Jan A., Bauer, Gerhard
Published in Blood

GWAS meta-analysis of over 29,000 people with epilepsy identifies 26 risk loci and subtype-specific genetic architecture

by Campbell, Ciarán, Chen, Siwei, Andrade, Danielle M, Annesi, Grazia, Auce, Pauls, Bebek, Nerses, Berkovic, Samuel F, Beydoun, Ahmad, Blatt, Ilan, Borggraefe, Ingo, Bradfield, Jonathan P, Brody, Lawrence C, Canafoglia, Laura, Castellotti, Barbara, Cerrato, Felecia, Cherny, Stacey S, Cheung, Ching-Lung, Cole, Andrew J, Cossette, Patrick, Daly, Mark J, Dlugos, Dennis J, Doherty, Colin P, Ellis, Colin A, Feucht, Martha, Franceschetti, Silvana, French, Jacqueline A, Gambardella, Antonio, Granata, Tiziana, Guerrini, Renzo, Haas, Kevin F, Howrigan, Daniel P, Jamnadas-Khoda, Jennifer, Jehi, Lara, Kanai, Masahiro, Kantanen, Anne-Mari, Kara, Bülent, Kasperavičiūte, Dalia, Kasteleijn-Nolst Trenite, Dorothee, Kegele, Josua, King, Chontelle, Klein, Karl M, Korczyn, Amos D, Koupparis, Andreas, Krey, Ilona, Kurki, Mitja I, Lauxmann, Stephen, Leech, Stephanie L, Lehesjoki, Anna-Elina, Lesca, Gaetan, Leu, Costin, Lewin, Naomi, Lopes-Cendes, Iscia, Magnusson, Sigurdur, Marson, Anthony G, May, Patrick, McGraw, Christopher M, Mei, Davide, Montomoli, Martino, Mostacci, Barbara, Muccioli, Lorenzo, Müller-Schlüter, Karen, Neubauer, Bernd, Nothnagel, Michael, Pendziwiat, Manuela, Pondrelli, Federica, Powell, Rob H. W, Privitera, Michael, Ragona, Francesca, Regan, Brigid M, Sadleir, Lynette G, Sander, Josemir W, Scala, Marcello, Sham, Pak, Sheidley, Beth R, Shih, Jerry J, Smith, Michael C, Sonsma, Anja C. M, Sperling, Michael R, Stephani, Ulrich, Stewart, William C, Stipa, Carlotta, Striano, Pasquale, Tan, K. Meng, Thomas, G. Neil, Timonen, Oskari, Todaro, Marian, Topaloğlu, Pınar, Tumiene, Birute, Utkus, Algirdas, van Baalen, Andreas, Visscher, Frank, Weber, Yvonne G, Weisenberg, Judith, Widdess-Walsh, Peter, Wolff, Markus, Wolking, Stefan, Yapıcı, Zuhal, Zagaglia, Sara, Zara, Federico, Zhou, Wei
Published in Nature genetics